Saturday, July 23, 2016

Intensive vs Standard Blood Pressure Control and Cardiovascular Disease Outcomes in Adults Aged ≥75 Years. A Randomized Clinical Trial

INTRODUCTION
- In the United States, 75% of persons older than 75 years have hypertension, for whom cardiovascular disease complications are a leading cause of disability, morbidity, and mortality
- European guideline committees have recommended treatment initiation only above 160 mm Hg for persons aged 80 years or older
- US guideline, a report from the panel appointed to the Eighth Joint National Committee (JNC 8), recommended a SBP treatment target of 150 mm Hg for adults aged 60 years or older.
- However, a report from a minority of the members argued to retain the previously recommended SBP treatment goal of 140 mm Hg, highlighting the lack of consensus

- Whether treatment targets should consider factors such as frailty or functional status is also unknown
- Observational studies have noted differential associations among elevated blood pressure (BP) and cardiovascular disease, stroke, and mortality risk when analyses are stratified according to measures of functional status.
- A recent secondary analysis of the Systolic Hypertension in the Elderly Program showed that the benefit of antihypertensive therapy was limited to participants without a self-reported physical ability limitation.
- In contrast, analyses from the Hypertension in the Very Elderly Trial (HYVET) showed a consistent benefit with antihypertensive therapy on outcomes irrespective of frailty status.

The Systolic Blood Pressure Intervention Trial (SPRINT) recently reported that participants assigned to an intensive SBP treatment target of less than 120 mm Hg vs the standard SBP treatment goal of less than140mmHg had a 25% lower relative risk of major cardiovascular events and death, and a 27% lower relative risk of death from any cause.
- This trial was specifically funded to enhance recruitment of a prespecified subgroup of adults aged 75 years or older, and the study protocol (appears in Supplement 1) also included measures of functional status and frailty.
- This article details results for the prespecified subgroup of adults aged 75 years or older with hypertension.

OBJECTIVE

To evaluate the effects of intensive (<120 mm Hg) compared with standard (<140 mm Hg) SBP targets in persons aged 75 years or older with hypertension but without diabetes.

METHODOLOGY

Population
Inclusion:
- Increased risk for cardiovascular disease (based on a clinical or subclinical cardiovascular disease, chronic kidney disease [CKD], a 10-year Framingham General cardiovascular disease risk ≥15%, or age ≥75 years).

Exclusion:
- had type 2 diabetes, a history of stroke, symptomatic heart failure within the past 6 months or reduced left ventricular ejection fraction (<35%), a clinical diagnosis of or treatment for dementia, an expected survival of less than 3 years, unintentional weight loss (>10% of body weight) during the preceding 6 months, an SBP of less than 110 mm Hg following 1 minute of standing, or resided in a nursing home.

Study Measurements
- Sociodemographic data were collected at baseline, whereas both clinical and laboratory data were obtained at baseline and every 3 months
- Race and ethnicity information was obtained via self-report.
- Blood pressure was determined using the mean of 3 properly sized automated cuff readings, taken 1 minute apart after 5 minutes of quiet rest without staff in the room.
- Gait speed was measured via a timed 4-m walk performed twice at the participant’s usual pace from a standing start.
- The use of an assistive device was permitted if typically used by the participant to walk short distances.
- The faster of the 2 gait speeds (measured in meters/second) was used in the analysis.
- Frailty status at randomization was quantified using a previously reported 37-item frailty index.

Clinical Outcomes
- A committee unaware of treatment assignment adjudicated the protocol-specified clinical outcomes.
- The primary cardiovascular disease outcome was a composite of: nonfatal myocardial infarction, acute coronary syndrome not resulting in a myocardial infarction, nonfatal stroke, nonfatal acute decompensated heart failure, and death from cardiovascular causes.
- Secondary outcomes: all-cause mortality and the composite of the SPRINT primary outcome and all-cause mortality.
- The primary renal disease outcome was assessed in participants with CKD at baseline (estimated glomerular filtration rate [eGFR] <60 ml/min/1.73 m2 based on the 4-variable
Modification of Diet in Renal Disease equation). It was based on the composite incidence of either a decrease in eGFR of 50% or greater (confirmed by subsequent laboratory test ≥90 days later) or the development of end-stage renal disease requiring long-term dialysis or transplantation.
- Secondary renal disease outcome (assessed in participants without CKD at baseline) was based on incidence of a decrease in eGFR from 30% or greater at baseline to a value less than 60 mL/min/1.73 m2 (also confirmed by a subsequent test ≥90 days later).

Definition of Serious Adverse Events
- Serious adverse events (SAEs) were defined as events that were fatal or life threatening, resulted in significant or persistent disability, required hospitalization or resulted in prolonged hospitalization, or medical events that the investigator judged to be a significant hazard or harm to the participant and required medical or surgical intervention to prevent any of these.
- The following conditions of interest were reported as adverse events if they were evaluated in an emergency department: hypotension, syncope, injurious falls, electrolyte abnormalities, and bradycardia.
- Episodes of acute kidney injury (or acute renal failure) were monitored if they led to hospitalization and were reported in the hospital discharge summary.

Statistical Analysis
- Power to detect a 25% treatment effect for the primary outcome within the subgroup of participants aged 75 years or older was estimated assuming an enrollment of 3250.With a 2-year recruitment period, maximum follow-up of 6 years, and annual loss to follow-up of 2%, power was estimated to be 81.9%, assuming an event rate of 3.25%per year in the standard treatment group (Appendix B in Supplement 1).

- Linear-mixed models with an unstructured covariance matrix, assuming independence across participants, were used to model longitudinal differences in SBP between treatment groups
- Fixed effects in the model were BP at randomization and a treatment group indicator.
- The time to first occurrence of the primary composite outcome, all-cause mortality, primary composite outcome plus all-cause mortality, SAEs, and loss to follow-up or withdrawing consent were compared between the 2 randomized groups using Cox proportional hazards regression models with the baseline hazard function stratified by clinic site (participants were recruited at 100 clinics).
- Follow-up time was censored on the date of last event ascertainment on or before August 20, 2015, the date on which the National Heart, Lung, and Blood Institute director decided to stop the intervention.

- Exploratory secondary analyses were conducted to examine modification of the treatment effect by frailty status and gait speed.
- Neither frailty status nor gait speed was a prespecified subgroup in the trial protocol.
We fit separate Cox regression models:
- for frailty status classified as fit (frailty index ≤0.10), less fit (frailty index >0.10 to ≤0.21), or frail (frailty index >0.21), and
- for gait speed classified as 0.8m/s or greater (normal walker), less than 0.8 m/s (slow walker), or missing.
- Interactions between treatment group, frailty status, and gait speed were formally tested by including interaction terms within a Cox regression model (ie, using likelihood ratio tests to compare with a model that did not allow the treatment effect to vary by frailty status or gait speed).
- For the primary cardiovascular disease composite outcome, sensitivity analyses accounting for the competing risk of death were conducted using the sub-distribution hazard model of Fine and Gray.
- All hypothesis tests were 2-sided at the 5%level of significance

- Additional analyses compared the total burden of SAEs between the randomized groups (allowing for recurrent events) using the mean cumulative count estimator (standard errors computed using bootstrap resampling).
- Hazard ratios (HRs) were computed to compare the randomized groups using the gap-time formation of the Prentice, Williams, and Peterson recurrent events regression model.
- All analyses were performed using SAS version 9.4 (SAS Institute Inc) and the R Statistical Computing Environment (http://www.r-project.org)

RESULTS

Baseline characteristics and Study Retention
- The treatment groups were similar for most characteristics with the exception of frailty status and aspirin use (Table 1).
- Overall, 815 participants (30.9%) were classified as frail and 1456 (55.2%) as less fit (Table 1).
- A total of 2510 (95.2%) participants provided complete follow-up data.

- In the intensive treatment group, 440 participants (33.4%) were classified as frail compared with 375 participants (28.4%) in the standard treatment group.
- A total of 740 participants (28.1%) were classified as slow walkers (<0.8m/s).
- There was no baseline treatment group difference in the proportion of participants classified as slow walkers or in performance on the Montreal Cognitive Assessment screening test

- Even though participants who were less fit, frail, or with reduced gait speed exhibited higher rates of loss to follow-up or withdrawal of consent, there were no significant differences between the treatment groups for frailty or low gait speed (eTable 1 in Supplement 2).
- The frequency at which participants discontinued the intervention but continued follow-up was 6.2% in the intensive treatment group vs 6.4% in the standard treatment group (P = .87).


Blood Pressure Levels
Throughout follow-up,
Mean SBP:
- Intensive treatment group: 123.4 mm Hg
- Standard treatment group: 134.8 mm Hg
- Between group difference: 11.4 mg (95% CI, 10.8-11.9 mm Hg)

Mean Diastolic BP:
- Intensive treatment group: 62.0 mm Hg
- Standard treatment group: 67.2 mm Hg

- On average, participants in the intensive treatment group required 1 more medication to reach the achieved lower BP (eTable 2 and eFigure 1 in Supplement 2).
- Within the intensive treatment group, mean SBP during follow-up was higher for participants classified as less fit or frail compared with those considered fit.

- Differences in mean SBP by treatment group differed by frailty status (P = .01), with frail participants exhibiting smaller inter-treatment group differences (10.8 mm Hg) compared with less fit participants (11.3 mm Hg) and fit participants (13.5 mm Hg).
- Treatment group differences in SBP were similar across subgroups defined by gait speed.


Clinical Outcome
- A primary composite outcome event was observed for 102 participants (2.59% per year) in the intensive treatment group and for 148 participants (3.85% per year) in the standard treatment group (HR, 0.66 [95% CI, 0.51-0.85]; Table 3).
- Results were similar for all-cause mortality (there were 73 deaths in the intensive treatment group and 107 deaths in the standard treatment group; HR, 0.67 [95% CI, 0.49-0.91]).
- Inference for the primary outcome was unchanged when non-cardiovascular disease death was treated as a competing risk (HR, 0.66 [95% CI, 0.52-0.85]).
- At 3.14 years, the number needed to treat (NNT) estimate for the primary outcome was 27 (95% CI, 19-61) and for all-cause mortality was 41 (95% CI, 27-145).
 - Because the treatment effect estimate was not statistically significant for cardiovascular disease death, the NNT estimate (using the abbreviations of Altman) was an NNTBenefit of 116 (NNTHarm of 544 to ∞ to NNTBenefit of 68).


- In participants without CKD at the time of randomization, more participants in the intensive treatment group compared with the standard treatment group experienced the secondary CKD outcome (a 30% decrease in eGFR from baseline to an eGFR <60 mL/min/1.73 m2 [1.70% vs 0.58% per year, respectively]; HR, 3.14 [95% CI, 1.66-6.37]).
- There were no significant treatment group differences in the primary renal outcome in those with baseline CKD; however, power to detect differences was limited due to low numbers of events.

Exploratory Subgroup Analyses
- Results stratified by baseline frailty status showed higher event rates with increasing frailty in both treatment groups (Table 4 and Figure 2).
- However, within each frailty stratum, absolute event rates were lower for the intensive treatment group (P = .84 for interaction).
- Results were similar when participants were stratified by gait speed (P = .85 for interaction), with the HRs in favor of the intensive treatment group in each gait speed stratum (eFigure 2 in Supplement 2).




Serious Adverse Events (SAEs)
- Detailed information regarding SAEs appears in eTable 3 and eTable 4 in Supplement 2.
- In the intensive treatment group, SAEs occurred in 637 participants (48.4%) compared with 637 participants (48.3%) in the standard treatment group (HR, 0.99 [95% CI, 0.89-1.11]; P = .90).
- The absolute rate of SAEs was higher but was not statistically significantly different in the intensive treatment group for hypotension (2.4%vs 1.4% in the standard treatment group;
For each specific SAE:
- Hypotension: 2.4% (intensive group) vs 1.4% (standard group) (HR, 1.71 [95% CI, 0.97-3.09])
- Syncope: 3.0% (intensive group) vs 2.4% (standard group) (HR, 1.23 [95% CI, 0.76-2.00])
- Electrolyte abnormalities: 4.0% (intensive group) vs 2.7% (standard group) (HR, 1.51 [95% CI, 0.99-2.33])
- Acute kidney injury: 5.5% (intensive group) vs 4.0% (standard group) (HR, 1.41 [95% CI, 0.98-2.04])
- Injurious falls: 4.9% (intensive group) vs 5.5% (standard group) (HR, 0.91 [95% CI, 0.65-1.29])
[Note from ZYL: To see whether the group differences are significant, we look at the 95% confidence interval (CI) of the hazard ratio (HR): If the CI pass did not pass through the value ‘1’, then it is significant; if the CI passed through value ‘1’, then it is not significant (The reason why we look at ‘1’ is because ‘1’ means null effect in ratio).
From the results, all of the CI of the serious adverse events reported passed through the value ‘1’, therefore the serious adverse events between groups were not significantly difference. However, it must be noted that there is a trend that the intensive group had more hypotension, electrolyte abnormalities and acute kidney injury (the lower CI is very near to 1)
- Even though the SAE rates were higher with greater frailty or slower walking speed, these rates were not statistically different by treatment group when stratified by frailty status or gait speed.

DISCUSSION

Main Findings
- These results extend and detail the main SPRINT study findings in community-dwelling persons aged 75 years or older, demonstrating that a treatment goal for SBP of <120 mm Hg reduced incident cardiovascular disease by 33% (from 3.85% to 2.59% per year) and total mortality by 32% (from 2.63% to 1.78% per year)
- Number needed to treat: strategy of intensive BP control for 3.14 years would be expected to prevent 1 primary outcome event for every 27 persons treated and 1 death from any cause for every 41 persons treated.
- These estimates are lower than those from the overall results of the trial due to the higher event rate in persons aged 75 years or older.
- Exploratory analysis also suggested that the benefit of intensive BP control was consistent among persons in this age range who were frail or had reduced gait speed.

Serious Adverse Events
- The overall SAE rate was comparable by treatment group, including among the most frail participants.
- There were no differences in the number of participants experiencing injurious falls or in the prevalence of orthostatic hypotension measured at study visits – complement results from other trials demonstrating improved BP control reduces risk for orthostatic hypotension and has no effect on risk for injurious falls

Limitations
- Randomization was not stratified by categories of age
- Did not enroll older adults residing in nursing homes, persons with type 2 diabetes or prevalent stroke (because of concurrent BP lowering trials) and individuals with symptomatic heart failure due to protocol differences required to maintain BP control in this condition – cannot be generalized to these groups of patients. Individuals with these conditions also represent a subset of older persons at increased risk for falls.

Exploratory Analysis
- No other chronic conditions were excluded from this trial, and the frailty index applied in this study combined with the assessment of gait speed contribute to assessing possible effect modification by comorbidity and functional status.
- In exploratory analyses, there was no evidence of heterogeneity for the cardiovascular benefit of intensive BP management by frailty or gait speed.
- However, these analyses should be interpreted cautiously.
- The analyses were not prespecified in the trial protocol and were possibly underpowered because SPRINT was designed to consider only the ability to detect a treatment effect in participants aged 75 years or older as a whole

Representativeness of the trial participants
- Despite excluding some chronic conditions, 30.9% of participants aged 75 years or older in this trial were categorized as frail at baseline, and the distribution of frailty status parallels that estimated for ambulatory, community living populations of similar age.
- In addition, the proportion of US adults aged 75 years or older who have hypertension and meet the study entry criteria has been estimated to represent 64% of that population using the 2007-2012 National Health and Nutrition Surveys (approximately 5.8 million individuals).
- Therefore, participants aged 75 years or older in this trial are representative of a sizeable fraction of adults in this age group with hypertension

Compare with the HYVET Trial
- Randomized 3845 patients aged 80 years or older within Europe and Asia (mean age, 83 years [3 years older than SPRINT]; mean entry SBP, 173mmHg [31 mm Hg higher than SPRINT]) to either therapy with indapamide, with or without the angiotensin-converting enzyme inhibitor perindopril, or placebo with an SBP treatment goal of <150 mm Hg.
- The 2-year between-group SBP difference was 15 mm Hg (the active treatment group achieved a mean SBP of 143mm Hg, slightly higher than the SPRINT baseline SBP).
- Similar to SPRINT, HYVET was terminated early (at a median follow-up time of 1.8 years) due to significant reductions in the incidence rate of total mortality.
- A retrospective analysis of the HYVET population conducted to determine its frailty status identified that (1) the cohort’s frailty status was similar to that of community living populations of similar age and (2) the treatment benefits were similar even in the most frail participants.
- Taken together, current results from SPRINT also reinforce and extend HYVET’s conclusions that risk reductions in cardiovascular disease events and mortality from high BP treatment are evident regardless of frailty status

SAEs related to Acute Kidney Injury
- Among all participants aged 75 years or older, the SAEs related to acute kidney injury occurred more frequently in the intensive treatment group (72 participants [5.5%] vs 53 participants [4.0%] in the standard treatment group).
- The differences in adverse renal outcomes may be related to a reversible intrarenal hemodynamic effect of the reduction in BP and more frequent use of diuretics, angiotensin-converting enzyme inhibitors, and angiotensin II receptor blockers in the intensive treatment group.
- Although there is no evidence of permanent kidney injury associated with the lower BP goal, the possibility of long-term adverse renal outcomes cannot be excluded and requires longer-term follow-up

Implications of the study
- Considering the high prevalence of hypertension among older persons, patients and their physicians may be inclined to underestimate the burden of hypertension or the benefits of lowering BP, resulting in under-treatment.
- On average, the benefits that resulted from intensive therapy required treatment with 1 additional antihypertensive drug and additional early visits for dose titration and monitoring.
- Future analyses of SPRINT data may be helpful to better define the burden, costs, and benefits of intensive BP control.
- However, the present results have substantial implications for the future of intensive BP therapy in older adults because of this condition’s high prevalence, the high absolute risk for cardiovascular disease complications from elevated BP, and the devastating consequences of such events on the independent function of older people

CONCLUSIONS
- Among ambulatory adults aged 75 years or older, treating to an SBP target of less than 120 mm Hg compared with an SBP target of less than 140 mm Hg resulted in significantly lower rates of fatal and nonfatal major cardiovascular events and death from any cause
- The overall serious adverse events rate was comparable by treatment group, including among the most frail participants.



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